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KEVEYIS (Primary Periodic Paralysis)
Patient Resources
UPLIZNA (Neuromyelitis Optica Spectrum Disorder)
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WAKIX (Narcolepsy)
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ARIKAYCE (MAC Lung Disease)
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DOJOLVI (Long-Chain Fatty Acid Oxidation Disorders)
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VIGADRONE (Infantile Spasms)
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STRENSIQ (Hypophosphatasia)
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QINLOCK (Gastrointestional Stromal Tumors)
Patient Resources
AYVAKIT (Gastrointestional Stromal Tumors)
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TRIPTODUR (Central Precocious Puberty)
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